Rare Diseases Clinical Trials in Brazil

Clinical Trials in: Mexico, Argentina, Colombia and Brazil.

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As a leading CRO in LATAM, we specialize in supporting clinical trials throughout the region. Our extensive experience and broad network of clinical sites enable us to execute trials with speed and efficiency, ensuring high patient recruitment and retention rates.

Rare Diseases Clinical Trials in Brazil

Rare Diseases Clinical Trials in Brazil – Clinical Trials LATAM

Rare diseases present unique challenges due to their low prevalence and limited treatment options. Clinical trials offer hope to patients and their families by providing opportunities for innovative therapies and advancing medical research. In recent years, Brazil has emerged as a prominent player in rare diseases clinical trials, making significant progress in improving patient outcomes and contributing to scientific knowledge.

This blog post aims to explore the importance of rare diseases clinical trials in Brazil, highlighting the advancements made, challenges faced, and the potential they hold for transforming the lives of individuals affected by rare diseases.

The Significance of Rare Diseases Clinical Trials

Rare diseases, although individually rare, collectively affect millions of individuals worldwide. Clinical trials play a crucial role in advancing our understanding of these conditions, exploring new treatment options, and improving patient care.

For individuals living with rare diseases, clinical trials offer a glimmer of hope, providing access to cutting-edge therapies and the opportunity to contribute to scientific advancements.

Brazil has recognized the significance of rare diseases clinical trials in improving patient outcomes and promoting research and development. By conducting clinical trials, Brazil not only contributes to the global knowledge base but also offers potential treatment options for patients who may have limited access to healthcare resources.

Progress in Rare Diseases Clinical Trials in Brazil

Brazil has made significant progress in establishing itself as a key hub for rare diseases clinical trials. The country has a well-regulated framework overseen by the National Health Surveillance Agency (ANVISA), ensuring patient safety, ethical standards, and scientific rigor throughout the research process.

ANVISA plays a pivotal role in approving and monitoring clinical trials, fostering an environment conducive to research and innovation.

Collaboration between academic institutions, research organizations, and healthcare facilities has been instrumental in driving the progress of rare diseases clinical trials in Brazil.

Institutions such as the Oswaldo Cruz Foundation (FIOCRUZ) and the Brazilian Association of Rare Diseases have actively promoted research and clinical trials. Moreover, partnerships with international organizations and research networks have facilitated knowledge exchange, resource sharing, and access to global expertise.

Brazil has also established specialized centers and research networks dedicated to rare diseases. These centers serve as vital hubs for diagnosis, treatment, and patient support. They bring together multidisciplinary teams of experts, fostering collaboration among researchers, healthcare professionals, and patient advocacy groups.

Rare Diseases Clinical Trials in Brazil

Rare Diseases Clinical Trials in Brazil

Rare Diseases Clinical Trials in Brazil

Challenges and Future Directions

While Brazil has made significant strides in rare diseases clinical trials, several challenges persist. Limited awareness and understanding among the general public, healthcare professionals, and policymakers remain significant barriers.

Efforts should be made to increase public awareness and education about rare diseases, their impact on individuals and families, and the importance of clinical trials in developing effective treatments.

Another challenge is the need for increased funding for rare diseases research. Brazil should prioritize allocating sufficient resources to support infrastructure, equipment, and training programs for researchers. Strengthening public-private partnerships and engaging philanthropic initiatives can help bridge the funding gap and promote sustainable research efforts.

To further enhance rare diseases clinical trials in Brazil, it is crucial to strengthen international collaborations. By participating in multinational trials and sharing expertise and resources, Brazil can expand its research capabilities and contribute to the development of innovative therapies for rare diseases.


Rare diseases pose significant challenges to individuals, families, and healthcare systems worldwide. Brazil has made commendable progress in rare diseases clinical trials, recognizing the importance of research in improving patient outcomes and fostering scientific advancements.

With a robust regulatory framework, collaboration between institutions, and specialized centers dedicated to rare diseases, Brazil is poised to continue advancing its capabilities in this field.To overcome the challenges ahead, Brazil must prioritize raising public awareness, securing adequate funding, and strengthening international collaborations.

Rare Diseases Clinical Trials in Brazil

Source: Duke Clinical Research Institute

Rare Diseases Clinical Trials in Brazil

Welcome to Cohortias!

of Latin America

Simplify Your Clinical Trials with Our Expert Infrastructure in Latin America

Say goodbye to the complex, costly, and disorganized process of conducting clinical trials. Our infrastructure in Latin America streamlines the launch of studies and ensures adherence to international standards. Schedule a call with us today to discover the path to simplified clinical research in Latin America.

Rare Diseases Clinical Trials in Brazil

Explore What We Are Doing Better

We define ourselves as a unique team, capable of blending our academic background with a global business mindset to bring the highest standard of quality and operational excellence into clinical research in Latin America.

Early Phase Trials

- First-in-Human Studies.
- Get to patients faster, no IND necessary.
- Valid data for FDA submission.

Rescue Studies

- Regain lost time and boost patient recruitment.
- We work alongside Global CROs to get studies back on track.
- More than 200 sites available.

Phase II & III Trials

- Full-Service Clinical Outsourcing.
- Proven infrastructure that can handle any trial.
- Local Regulatory Experts
- Wide network of sites and physicians.

Medical Devices

- A fast-track platform that will meet your timeline.
- We take care of everything, from shipping requirements all the way to data collection.
Rare Diseases Clinical Trials in Brazil

Full Service CRO in LATAM

Outsourcing Clinical Trials to Latin America

Unlock the advantages and opportunities of outsourcing clinical trials to Latin America. Diverse patient population, streamlined regulations, and cost-effectiveness

Lower Operating Costs

From lower labor costs to lower costs for rent, utilities, and equipment, you can save money on your clinical trial budget while still ensuring the quality of your trial

Access to Emerging Markets

Latin America offers access to emerging markets, providing an opportunity for pharmaceutical companies to expand their reach and reach new patient populations.

Rare Diseases Clinical Trials in Brazil

Cohortias is redefining Clinical Research in Latin America

We are committed to become leaders in providing clinical research services in Latin America. Here at Cohortias, we combine our academic roots, proven experience and a large pool of patients from an extensive network of sites.

Our main purpose is to deliver high quality data.

Rare Diseases Clinical Trials in Brazil

Clinical Research in Latin America

Cohortias has built an extensive and highly reputable network of clinical sites which can access patients in a timely manner and operate within a standard-of-care comparable to the U.S. healthcare system.


  • Site Management

  • Data Management

  • Site Selection

  • Regulatory Submissions

  • Clinical Monitoring

  • Protocol Development


Beta Trials Platform

  • First-in-human studies

Medical Devices

  • Pilot and Pivotal Device Studies

Phases I – III

  • We partner with our clients to bring their products in a fast and efficient manner to the market with the highest quality standards


  • Diabetes/Metabolic Syndromes
  • Infectious Diseases
  • Cardiovascular
  • Neurology
  • Respiratory
  • Oncology

Rare Diseases Clinical Trials in Brazil

Clinical Research in Latin America

Academic Leadership and Extensive Clinical Site Network for Efficient Clinical Trials

  • Our peer-to-peer management approach guarantees high patient recruitment and retention in any clinical trial

High Speed Execution

  • We offer the quickest start-up times in each country.
  • Efficient Clinical Site Selection and Contracting.
  • Benefit from our extensive network of clinical sites and streamlined contracting process.

Operational Excellence

  • Proven record of delivering rescue studies, we consistently exceed industry performance standards.
  • Our team provides efficient query resolution to keep your trial on track.

Business Insight and Flexibility

  • We offer innovative pricing models and short lines of communication to ensure maximum flexibility and cost-effectiveness.
  • At Cohortias, we prioritize  short lines of communication to ensure efficient collaboration.
  • Swift adaptation to changes in the trial landscape to keep your study on schedule.

Rare Diseases Clinical Trials in Brazil

We provide our services with offices in:

Colombia &

Daniela Maresca
Daniela Maresca | Country Lead Argentina
Martín Hernández-Torre | CMO
Maritza Rojas | CRA II
Pedro Alvarez | Business Development Manager
Samantha Rodriguez Cohortias
Samantha Rdz. | Start-Up Manager
Rare Diseases Clinical Trials in Brazil

The Cohortias Team

Rare Diseases Clinical Trials in Brazil

As the largest South American Contract research Organization, we know the Advantages and Challenges Of the Region

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Rare Diseases Clinical Trials in Brazil

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